Ascendis Wins FDA Approval for Achondroplasia Drug, Waits on EU Action
The FDA on Friday granted approval to Ascendis Pharma for its once-weekly treatment, navepegritide, aimed at addressing achondroplasia, a genetic disorder resulting in dwarfism. This pivotal decision marks a significant milestone for Ascendis, positioning it within a competitive landscape that may soon feature multiple players targeting this rare condition. The approval of navepegritide not only…









