FDA Expands Vertex’s Casgevy Label to Include Patients as Young as 2
Vertex Pharmaceuticals has received FDA approval for a label expansion of its gene therapy Casgevy, now permitting treatment for children aged 2 and older suffering from sickle cell disease or transfusion-dependent beta thalassemia. Previously, the therapy was only available to patients aged 12 and above, marking a significant shift in treatment accessibility. This expansion reflects…









